Index
1 Rare Disease Drug Market Overview
1.1 Product Overview and Scope of Rare Disease Drug
1.2 Rare Disease Drug Segment by Type
1.2.1 Global Rare Disease Drug Market Value Comparison by Type (2024-2030)
1.2.2 Above 1‰
1.2.3 0.65‰~1‰
1.2.4 Below 0.1‰
1.3 Rare Disease Drug Segment by Application
1.3.1 Global Rare Disease Drug Market Value by Application: (2024-2030)
1.3.2 Hospital Pharmacies
1.3.3 Speciality Pharmacies
1.3.4 Retail pharmacies
1.3.5 Others
1.4 Global Rare Disease Drug Market Size Estimates and Forecasts
1.4.1 Global Rare Disease Drug Revenue 2019-2030
1.4.2 Global Rare Disease Drug Sales 2019-2030
1.4.3 Global Rare Disease Drug Market Average Price (2019-2030)
1.5 Assumptions and Limitations
2 Rare Disease Drug Market Competition by Manufacturers
2.1 Global Rare Disease Drug Sales Market Share by Manufacturers (2019-2024)
2.2 Global Rare Disease Drug Revenue Market Share by Manufacturers (2019-2024)
2.3 Global Rare Disease Drug Average Price by Manufacturers (2019-2024)
2.4 Global Rare Disease Drug Industry Ranking 2022 VS 2023 VS 2024
2.5 Global Key Manufacturers of Rare Disease Drug, Manufacturing Sites & Headquarters
2.6 Global Key Manufacturers of Rare Disease Drug, Product Type & Application
2.7 Rare Disease Drug Market Competitive Situation and Trends
2.7.1 Rare Disease Drug Market Concentration Rate
2.7.2 The Global Top 5 and Top 10 Largest Rare Disease Drug Players Market Share by Revenue
2.7.3 Global Rare Disease Drug Market Share by Company Type (Tier 1, Tier 2 and Tier 3)
2.8 Manufacturers Mergers & Acquisitions, Expansion Plans
3 Rare Disease Drug Retrospective Market Scenario by Region
3.1 Global Rare Disease Drug Market Size by Region: 2019 Versus 2023 Versus 2030
3.2 Global Rare Disease Drug Global Rare Disease Drug Sales by Region: 2019-2030
3.2.1 Global Rare Disease Drug Sales by Region: 2019-2024
3.2.2 Global Rare Disease Drug Sales by Region: 2025-2030
3.3 Global Rare Disease Drug Global Rare Disease Drug Revenue by Region: 2019-2030
3.3.1 Global Rare Disease Drug Revenue by Region: 2019-2024
3.3.2 Global Rare Disease Drug Revenue by Region: 2025-2030
3.4 North America Rare Disease Drug Market Facts & Figures by Country
3.4.1 North America Rare Disease Drug Market Size by Country: 2019 VS 2023 VS 2030
3.4.2 North America Rare Disease Drug Sales by Country (2019-2030)
3.4.3 North America Rare Disease Drug Revenue by Country (2019-2030)
3.4.4 U.S.
3.4.5 Canada
3.5 Europe Rare Disease Drug Market Facts & Figures by Country
3.5.1 Europe Rare Disease Drug Market Size by Country: 2019 VS 2023 VS 2030
3.5.2 Europe Rare Disease Drug Sales by Country (2019-2030)
3.5.3 Europe Rare Disease Drug Revenue by Country (2019-2030)
3.5.4 Germany
3.5.5 France
3.5.6 U.K.
3.5.7 Italy
3.5.8 Russia
3.6 Asia Pacific Rare Disease Drug Market Facts & Figures by Country
3.6.1 Asia Pacific Rare Disease Drug Market Size by Country: 2019 VS 2023 VS 2030
3.6.2 Asia Pacific Rare Disease Drug Sales by Country (2019-2030)
3.6.3 Asia Pacific Rare Disease Drug Revenue by Country (2019-2030)
3.6.4 China
3.6.5 Japan
3.6.6 South Korea
3.6.7 India
3.6.8 Australia
3.6.9 Taiwan
3.6.10 Indonesia
3.6.11 Thailand
3.6.12 Malaysia
3.6.13 Philippines
3.7 Latin America Rare Disease Drug Market Facts & Figures by Country
3.7.1 Latin America Rare Disease Drug Market Size by Country: 2019 VS 2023 VS 2030
3.7.2 Latin America Rare Disease Drug Sales by Country (2019-2030)
3.7.3 Latin America Rare Disease Drug Revenue by Country (2019-2030)
3.7.4 Mexico
3.7.5 Brazil
3.7.6 Argentina
3.8 Middle East and Africa Rare Disease Drug Market Facts & Figures by Country
3.8.1 Middle East and Africa Rare Disease Drug Market Size by Country: 2019 VS 2023 VS 2030
3.8.2 Middle East and Africa Rare Disease Drug Sales by Country (2019-2030)
3.8.3 Middle East and Africa Rare Disease Drug Revenue by Country (2019-2030)
3.8.4 Turkey
3.8.5 Saudi Arabia
3.8.6 U.A.E
4 Segment by Type
4.1 Global Rare Disease Drug Sales by Type (2019-2030)
4.1.1 Global Rare Disease Drug Sales by Type (2019-2024)
4.1.2 Global Rare Disease Drug Sales by Type (2025-2030)
4.1.3 Global Rare Disease Drug Sales Market Share by Type (2019-2030)
4.2 Global Rare Disease Drug Revenue by Type (2019-2030)
4.2.1 Global Rare Disease Drug Revenue by Type (2019-2024)
4.2.2 Global Rare Disease Drug Revenue by Type (2025-2030)
4.2.3 Global Rare Disease Drug Revenue Market Share by Type (2019-2030)
4.3 Global Rare Disease Drug Price by Type (2019-2030)
5 Segment by Application
5.1 Global Rare Disease Drug Sales by Application (2019-2030)
5.1.1 Global Rare Disease Drug Sales by Application (2019-2024)
5.1.2 Global Rare Disease Drug Sales by Application (2025-2030)
5.1.3 Global Rare Disease Drug Sales Market Share by Application (2019-2030)
5.2 Global Rare Disease Drug Revenue by Application (2019-2030)
5.2.1 Global Rare Disease Drug Revenue by Application (2019-2024)
5.2.2 Global Rare Disease Drug Revenue by Application (2025-2030)
5.2.3 Global Rare Disease Drug Revenue Market Share by Application (2019-2030)
5.3 Global Rare Disease Drug Price by Application (2019-2030)
6 Key Companies Profiled
6.1 Novartis AG
6.1.1 Novartis AG Corporation Information
6.1.2 Novartis AG Description and Business Overview
6.1.3 Novartis AG Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.1.4 Novartis AG Rare Disease Drug Product Portfolio
6.1.5 Novartis AG Recent Developments/Updates
6.2 Bristol-Myers Squibb Company
6.2.1 Bristol-Myers Squibb Company Corporation Information
6.2.2 Bristol-Myers Squibb Company Description and Business Overview
6.2.3 Bristol-Myers Squibb Company Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.2.4 Bristol-Myers Squibb Company Rare Disease Drug Product Portfolio
6.2.5 Bristol-Myers Squibb Company Recent Developments/Updates
6.3 Celgene Corporation
6.3.1 Celgene Corporation Corporation Information
6.3.2 Celgene Corporation Description and Business Overview
6.3.3 Celgene Corporation Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.3.4 Celgene Corporation Rare Disease Drug Product Portfolio
6.3.5 Celgene Corporation Recent Developments/Updates
6.4 F. Hoffmann-La Roche Ltd.
6.4.1 F. Hoffmann-La Roche Ltd. Corporation Information
6.4.2 F. Hoffmann-La Roche Ltd. Description and Business Overview
6.4.3 F. Hoffmann-La Roche Ltd. Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.4.4 F. Hoffmann-La Roche Ltd. Rare Disease Drug Product Portfolio
6.4.5 F. Hoffmann-La Roche Ltd. Recent Developments/Updates
6.5 Pfizer, Inc.
6.5.1 Pfizer, Inc. Corporation Information
6.5.2 Pfizer, Inc. Description and Business Overview
6.5.3 Pfizer, Inc. Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.5.4 Pfizer, Inc. Rare Disease Drug Product Portfolio
6.5.5 Pfizer, Inc. Recent Developments/Updates
6.6 Sanofi S.A.
6.6.1 Sanofi S.A. Corporation Information
6.6.2 Sanofi S.A. Description and Business Overview
6.6.3 Sanofi S.A. Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.6.4 Sanofi S.A. Rare Disease Drug Product Portfolio
6.6.5 Sanofi S.A. Recent Developments/Updates
6.7 Alexion Pharmaceuticals, Inc.
6.6.1 Alexion Pharmaceuticals, Inc. Corporation Information
6.6.2 Alexion Pharmaceuticals, Inc. Description and Business Overview
6.6.3 Alexion Pharmaceuticals, Inc. Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.4.4 Alexion Pharmaceuticals, Inc. Rare Disease Drug Product Portfolio
6.7.5 Alexion Pharmaceuticals, Inc. Recent Developments/Updates
6.8 Eli Lilly and Company
6.8.1 Eli Lilly and Company Corporation Information
6.8.2 Eli Lilly and Company Description and Business Overview
6.8.3 Eli Lilly and Company Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.8.4 Eli Lilly and Company Rare Disease Drug Product Portfolio
6.8.5 Eli Lilly and Company Recent Developments/Updates
6.9 Novo Nordisk A/S
6.9.1 Novo Nordisk A/S Corporation Information
6.9.2 Novo Nordisk A/S Description and Business Overview
6.9.3 Novo Nordisk A/S Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.9.4 Novo Nordisk A/S Rare Disease Drug Product Portfolio
6.9.5 Novo Nordisk A/S Recent Developments/Updates
6.10 AstraZeneca
6.10.1 AstraZeneca Corporation Information
6.10.2 AstraZeneca Description and Business Overview
6.10.3 AstraZeneca Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.10.4 AstraZeneca Rare Disease Drug Product Portfolio
6.10.5 AstraZeneca Recent Developments/Updates
6.11 Eisai Co., Ltd.
6.11.1 Eisai Co., Ltd. Corporation Information
6.11.2 Eisai Co., Ltd. Rare Disease Drug Description and Business Overview
6.11.3 Eisai Co., Ltd. Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.11.4 Eisai Co., Ltd. Rare Disease Drug Product Portfolio
6.11.5 Eisai Co., Ltd. Recent Developments/Updates
6.12 Daiichi Sankyo Company Limited
6.12.1 Daiichi Sankyo Company Limited Corporation Information
6.12.2 Daiichi Sankyo Company Limited Rare Disease Drug Description and Business Overview
6.12.3 Daiichi Sankyo Company Limited Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.12.4 Daiichi Sankyo Company Limited Rare Disease Drug Product Portfolio
6.12.5 Daiichi Sankyo Company Limited Recent Developments/Updates
6.13 Bayer AG
6.13.1 Bayer AG Corporation Information
6.13.2 Bayer AG Rare Disease Drug Description and Business Overview
6.13.3 Bayer AG Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.13.4 Bayer AG Rare Disease Drug Product Portfolio
6.13.5 Bayer AG Recent Developments/Updates
6.14 GlaxoSmithKline
6.14.1 GlaxoSmithKline Corporation Information
6.14.2 GlaxoSmithKline Rare Disease Drug Description and Business Overview
6.14.3 GlaxoSmithKline Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.14.4 GlaxoSmithKline Rare Disease Drug Product Portfolio
6.14.5 GlaxoSmithKline Recent Developments/Updates
6.15 Merck & Co., Inc.
6.15.1 Merck & Co., Inc. Corporation Information
6.15.2 Merck & Co., Inc. Rare Disease Drug Description and Business Overview
6.15.3 Merck & Co., Inc. Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.15.4 Merck & Co., Inc. Rare Disease Drug Product Portfolio
6.15.5 Merck & Co., Inc. Recent Developments/Updates
6.16 Johnson & Johnson
6.16.1 Johnson & Johnson Corporation Information
6.16.2 Johnson & Johnson Rare Disease Drug Description and Business Overview
6.16.3 Johnson & Johnson Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.16.4 Johnson & Johnson Rare Disease Drug Product Portfolio
6.16.5 Johnson & Johnson Recent Developments/Updates
6.17 Biogen, Inc.
6.17.1 Biogen, Inc. Corporation Information
6.17.2 Biogen, Inc. Rare Disease Drug Description and Business Overview
6.17.3 Biogen, Inc. Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.17.4 Biogen, Inc. Rare Disease Drug Product Portfolio
6.17.5 Biogen, Inc. Recent Developments/Updates
6.18 Takeda
6.18.1 Takeda Corporation Information
6.18.2 Takeda Rare Disease Drug Description and Business Overview
6.18.3 Takeda Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.18.4 Takeda Rare Disease Drug Product Portfolio
6.18.5 Takeda Recent Developments/Updates
6.19 Amgen, Inc.
6.19.1 Amgen, Inc. Corporation Information
6.19.2 Amgen, Inc. Rare Disease Drug Description and Business Overview
6.19.3 Amgen, Inc. Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.19.4 Amgen, Inc. Rare Disease Drug Product Portfolio
6.19.5 Amgen, Inc. Recent Developments/Updates
6.20 Deciphera
6.20.1 Deciphera Corporation Information
6.20.2 Deciphera Rare Disease Drug Description and Business Overview
6.20.3 Deciphera Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.20.4 Deciphera Rare Disease Drug Product Portfolio
6.20.5 Deciphera Recent Developments/Updates
6.21 Atara Biotherapeutics
6.21.1 Atara Biotherapeutics Corporation Information
6.21.2 Atara Biotherapeutics Rare Disease Drug Description and Business Overview
6.21.3 Atara Biotherapeutics Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.21.4 Atara Biotherapeutics Rare Disease Drug Product Portfolio
6.21.5 Atara Biotherapeutics Recent Developments/Updates
6.22 ProQR
6.22.1 ProQR Corporation Information
6.22.2 ProQR Rare Disease Drug Description and Business Overview
6.22.3 ProQR Rare Disease Drug Sales, Revenue and Gross Margin (2019-2024)
6.22.4 ProQR Rare Disease Drug Product Portfolio
6.22.5 ProQR Recent Developments/Updates
7 Industry Chain and Sales Channels Analysis
7.1 Rare Disease Drug Industry Chain Analysis
7.2 Rare Disease Drug Key Raw Materials
7.2.1 Key Raw Materials
7.2.2 Raw Materials Key Suppliers
7.3 Rare Disease Drug Production Mode & Process
7.4 Rare Disease Drug Sales and Marketing
7.4.1 Rare Disease Drug Sales Channels
7.4.2 Rare Disease Drug Distributors
7.5 Rare Disease Drug Customers
8 Rare Disease Drug Market Dynamics
8.1 Rare Disease Drug Industry Trends
8.2 Rare Disease Drug Market Drivers
8.3 Rare Disease Drug Market Challenges
8.4 Rare Disease Drug Market Restraints
9 Research Finding and Conclusion
10 Methodology and Data Source
10.1 Methodology/Research Approach
10.1.1 Research Programs/Design
10.1.2 Market Size Estimation
10.1.3 Market Breakdown and Data Triangulation
10.2 Data Source
10.2.1 Secondary Sources
10.2.2 Primary Sources
10.3 Author List
10.4 Disclaimer
List of Tables
List of Tables
Table 1. Global Rare Disease Drug Market Value Comparison by Type (2024-2030) & (US$ Million)
Table 2. Global Rare Disease Drug Market Value Comparison by Application (2024-2030) & (US$ Million)
Table 3. Global Rare Disease Drug Market Competitive Situation by Manufacturers in 2023
Table 4. Global Rare Disease Drug Sales (K Doses) of Key Manufacturers (2019-2024)
Table 5. Global Rare Disease Drug Sales Market Share by Manufacturers (2019-2024)
Table 6. Global Rare Disease Drug Revenue (US$ Million) by Manufacturers (2019-2024)
Table 7. Global Rare Disease Drug Revenue Share by Manufacturers (2019-2024)
Table 8. Global Market Rare Disease Drug Average Price (USD/Dose) of Key Manufacturers (2019-2024)
Table 9. Global Key Players of Rare Disease Drug, Industry Ranking, 2022 VS 2023 VS 2024
Table 10. Global Key Manufacturers of Rare Disease Drug, Manufacturing Sites & Headquarters
Table 11. Global Key Manufacturers of Rare Disease Drug, Product Type & Application
Table 12. Global Key Manufacturers of Rare Disease Drug, Date of Enter into This Industry
Table 13. Global Manufacturers Market Concentration Ratio (CR5 and HHI)
Table 14. Global Rare Disease Drug by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Rare Disease Drug as of 2023)
Table 15. Manufacturers Mergers & Acquisitions, Expansion Plans
Table 16. Global Rare Disease Drug Market Size by Region (US$ Million): 2019 VS 2023 VS 2030
Table 17. Global Rare Disease Drug Sales by Region (2019-2024) & (K Doses)
Table 18. Global Rare Disease Drug Sales Market Share by Region (2019-2024)
Table 19. Global Rare Disease Drug Sales by Region (2025-2030) & (K Doses)
Table 20. Global Rare Disease Drug Sales Market Share by Region (2025-2030)
Table 21. Global Rare Disease Drug Revenue by Region (2019-2024) & (US$ Million)
Table 22. Global Rare Disease Drug Revenue Market Share by Region (2019-2024)
Table 23. Global Rare Disease Drug Revenue by Region (2025-2030) & (US$ Million)
Table 24. Global Rare Disease Drug Revenue Market Share by Region (2025-2030)
Table 25. North America Rare Disease Drug Revenue by Country: 2019 VS 2023 VS 2030 (US$ Million)
Table 26. North America Rare Disease Drug Sales by Country (2019-2024) & (K Doses)
Table 27. North America Rare Disease Drug Sales by Country (2025-2030) & (K Doses)
Table 28. North America Rare Disease Drug Revenue by Country (2019-2024) & (US$ Million)
Table 29. North America Rare Disease Drug Revenue by Country (2025-2030) & (US$ Million)
Table 30. Europe Rare Disease Drug Revenue by Country: 2019 VS 2023 VS 2030 (US$ Million)
Table 31. Europe Rare Disease Drug Sales by Country (2019-2024) & (K Doses)
Table 32. Europe Rare Disease Drug Sales by Country (2025-2030) & (K Doses)
Table 33. Europe Rare Disease Drug Revenue by Country (2019-2024) & (US$ Million)
Table 34. Europe Rare Disease Drug Revenue by Country (2025-2030) & (US$ Million)
Table 35. Asia Pacific Rare Disease Drug Revenue by Region: 2019 VS 2023 VS 2030 (US$ Million)
Table 36. Asia Pacific Rare Disease Drug Sales by Region (2019-2024) & (K Doses)
Table 37. Asia Pacific Rare Disease Drug Sales by Region (2025-2030) & (K Doses)
Table 38. Asia Pacific Rare Disease Drug Revenue by Region (2019-2024) & (US$ Million)
Table 39. Asia Pacific Rare Disease Drug Revenue by Region (2025-2030) & (US$ Million)
Table 40. Latin America Rare Disease Drug Revenue by Country: 2019 VS 2023 VS 2030 (US$ Million)
Table 41. Latin America Rare Disease Drug Sales by Country (2019-2024) & (K Doses)
Table 42. Latin America Rare Disease Drug Sales by Country (2025-2030) & (K Doses)
Table 43. Latin America Rare Disease Drug Revenue by Country (2019-2024) & (US$ Million)
Table 44. Latin America Rare Disease Drug Revenue by Country (2025-2030) & (US$ Million)
Table 45. Middle East & Africa Rare Disease Drug Revenue by Country: 2019 VS 2023 VS 2030 (US$ Million)
Table 46. Middle East & Africa Rare Disease Drug Sales by Country (2019-2024) & (K Doses)
Table 47. Middle East & Africa Rare Disease Drug Sales by Country (2025-2030) & (K Doses)
Table 48. Middle East & Africa Rare Disease Drug Revenue by Country (2019-2024) & (US$ Million)
Table 49. Middle East & Africa Rare Disease Drug Revenue by Country (2025-2030) & (US$ Million)
Table 50. Global Rare Disease Drug Sales (K Doses) by Type (2019-2024)
Table 51. Global Rare Disease Drug Sales (K Doses) by Type (2025-2030)
Table 52. Global Rare Disease Drug Sales Market Share by Type (2019-2024)
Table 53. Global Rare Disease Drug Sales Market Share by Type (2025-2030)
Table 54. Global Rare Disease Drug Revenue (US$ Million) by Type (2019-2024)
Table 55. Global Rare Disease Drug Revenue (US$ Million) by Type (2025-2030)
Table 56. Global Rare Disease Drug Revenue Market Share by Type (2019-2024)
Table 57. Global Rare Disease Drug Revenue Market Share by Type (2025-2030)
Table 58. Global Rare Disease Drug Price (USD/Dose) by Type (2019-2024)
Table 59. Global Rare Disease Drug Price (USD/Dose) by Type (2025-2030)
Table 60. Global Rare Disease Drug Sales (K Doses) by Application (2019-2024)
Table 61. Global Rare Disease Drug Sales (K Doses) by Application (2025-2030)
Table 62. Global Rare Disease Drug Sales Market Share by Application (2019-2024)
Table 63. Global Rare Disease Drug Sales Market Share by Application (2025-2030)
Table 64. Global Rare Disease Drug Revenue (US$ Million) by Application (2019-2024)
Table 65. Global Rare Disease Drug Revenue (US$ Million) by Application (2025-2030)
Table 66. Global Rare Disease Drug Revenue Market Share by Application (2019-2024)
Table 67. Global Rare Disease Drug Revenue Market Share by Application (2025-2030)
Table 68. Global Rare Disease Drug Price (USD/Dose) by Application (2019-2024)
Table 69. Global Rare Disease Drug Price (USD/Dose) by Application (2025-2030)
Table 70. Novartis AG Corporation Information
Table 71. Novartis AG Description and Business Overview
Table 72. Novartis AG Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 73. Novartis AG Rare Disease Drug Product
Table 74. Novartis AG Recent Developments/Updates
Table 75. Bristol-Myers Squibb Company Corporation Information
Table 76. Bristol-Myers Squibb Company Description and Business Overview
Table 77. Bristol-Myers Squibb Company Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 78. Bristol-Myers Squibb Company Rare Disease Drug Product
Table 79. Bristol-Myers Squibb Company Recent Developments/Updates
Table 80. Celgene Corporation Corporation Information
Table 81. Celgene Corporation Description and Business Overview
Table 82. Celgene Corporation Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 83. Celgene Corporation Rare Disease Drug Product
Table 84. Celgene Corporation Recent Developments/Updates
Table 85. F. Hoffmann-La Roche Ltd. Corporation Information
Table 86. F. Hoffmann-La Roche Ltd. Description and Business Overview
Table 87. F. Hoffmann-La Roche Ltd. Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 88. F. Hoffmann-La Roche Ltd. Rare Disease Drug Product
Table 89. F. Hoffmann-La Roche Ltd. Recent Developments/Updates
Table 90. Pfizer, Inc. Corporation Information
Table 91. Pfizer, Inc. Description and Business Overview
Table 92. Pfizer, Inc. Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 93. Pfizer, Inc. Rare Disease Drug Product
Table 94. Pfizer, Inc. Recent Developments/Updates
Table 95. Sanofi S.A. Corporation Information
Table 96. Sanofi S.A. Description and Business Overview
Table 97. Sanofi S.A. Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 98. Sanofi S.A. Rare Disease Drug Product
Table 99. Sanofi S.A. Recent Developments/Updates
Table 100. Alexion Pharmaceuticals, Inc. Corporation Information
Table 101. Alexion Pharmaceuticals, Inc. Description and Business Overview
Table 102. Alexion Pharmaceuticals, Inc. Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 103. Alexion Pharmaceuticals, Inc. Rare Disease Drug Product
Table 104. Alexion Pharmaceuticals, Inc. Recent Developments/Updates
Table 105. Eli Lilly and Company Corporation Information
Table 106. Eli Lilly and Company Description and Business Overview
Table 107. Eli Lilly and Company Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 108. Eli Lilly and Company Rare Disease Drug Product
Table 109. Eli Lilly and Company Recent Developments/Updates
Table 110. Novo Nordisk A/S Corporation Information
Table 111. Novo Nordisk A/S Description and Business Overview
Table 112. Novo Nordisk A/S Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 113. Novo Nordisk A/S Rare Disease Drug Product
Table 114. Novo Nordisk A/S Recent Developments/Updates
Table 115. AstraZeneca Corporation Information
Table 116. AstraZeneca Description and Business Overview
Table 117. AstraZeneca Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 118. AstraZeneca Rare Disease Drug Product
Table 119. AstraZeneca Recent Developments/Updates
Table 120. Eisai Co., Ltd. Corporation Information
Table 121. Eisai Co., Ltd. Description and Business Overview
Table 122. Eisai Co., Ltd. Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 123. Eisai Co., Ltd. Rare Disease Drug Product
Table 124. Eisai Co., Ltd. Recent Developments/Updates
Table 125. Daiichi Sankyo Company Limited Corporation Information
Table 126. Daiichi Sankyo Company Limited Description and Business Overview
Table 127. Daiichi Sankyo Company Limited Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 128. Daiichi Sankyo Company Limited Rare Disease Drug Product
Table 129. Daiichi Sankyo Company Limited Recent Developments/Updates
Table 130. Bayer AG Corporation Information
Table 131. Bayer AG Description and Business Overview
Table 132. Bayer AG Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 133. Bayer AG Rare Disease Drug Product
Table 134. Bayer AG Recent Developments/Updates
Table 135. GlaxoSmithKline Corporation Information
Table 136. GlaxoSmithKline Description and Business Overview
Table 137. GlaxoSmithKline Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 138. GlaxoSmithKline Rare Disease Drug Product
Table 139. GlaxoSmithKline Recent Developments/Updates
Table 140. Merck & Co., Inc. Corporation Information
Table 141. Merck & Co., Inc. Description and Business Overview
Table 142. Merck & Co., Inc. Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 143. Merck & Co., Inc. Rare Disease Drug Product
Table 144. Merck & Co., Inc. Recent Developments/Updates
Table 145. Johnson & Johnson Corporation Information
Table 146. Johnson & Johnson Description and Business Overview
Table 147. Johnson & Johnson Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 148. Johnson & Johnson Rare Disease Drug Product
Table 149. Johnson & Johnson Recent Developments/Updates
Table 150. Biogen, Inc. Corporation Information
Table 151. Biogen, Inc. Description and Business Overview
Table 152. Biogen, Inc. Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 153. Biogen, Inc. Rare Disease Drug Product
Table 154. Biogen, Inc. Recent Developments/Updates
Table 155. Takeda Corporation Information
Table 156. Takeda Description and Business Overview
Table 157. Takeda Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 158. Takeda Rare Disease Drug Product
Table 159. Takeda Recent Developments/Updates
Table 160. Amgen, Inc. Corporation Information
Table 161. Amgen, Inc. Description and Business Overview
Table 162. Amgen, Inc. Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 163. Amgen, Inc. Rare Disease Drug Product
Table 164. Amgen, Inc. Recent Developments/Updates
Table 165. Deciphera Corporation Information
Table 166. Deciphera Description and Business Overview
Table 167. Deciphera Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 168. Deciphera Rare Disease Drug Product
Table 169. Deciphera Recent Developments/Updates
Table 170. Atara Biotherapeutics Corporation Information
Table 171. Atara Biotherapeutics Description and Business Overview
Table 172. Atara Biotherapeutics Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 173. Atara Biotherapeutics Rare Disease Drug Product
Table 174. Atara Biotherapeutics Recent Developments/Updates
Table 175. ProQR Corporation Information
Table 176. ProQR Description and Business Overview
Table 177. ProQR Rare Disease Drug Sales (K Doses), Revenue (US$ Million), Price (USD/Dose) and Gross Margin (2019-2024)
Table 178. ProQR Rare Disease Drug Product
Table 179. ProQR Recent Developments/Updates
Table 180. Key Raw Materials Lists
Table 181. Raw Materials Key Suppliers Lists
Table 182. Rare Disease Drug Distributors List
Table 183. Rare Disease Drug Customers List
Table 184. Rare Disease Drug Market Trends
Table 185. Rare Disease Drug Market Drivers
Table 186. Rare Disease Drug Market Challenges
Table 187. Rare Disease Drug Market Restraints
Table 188. Research Programs/Design for This Report
Table 189. Key Data Information from Secondary Sources
Table 190. Key Data Information from Primary Sources
List of Figures
Figure 1. Product Picture of Rare Disease Drug
Figure 2. Global Rare Disease Drug Market Value Comparison by Type (2024-2030) & (US$ Million)
Figure 3. Global Rare Disease Drug Market Share by Type in 2023 & 2030
Figure 4. Above 1‰ Product Picture
Figure 5. 0.65‰~1‰ Product Picture
Figure 6. Below 0.1‰ Product Picture
Figure 7. Global Rare Disease Drug Market Value Comparison by Application (2024-2030) & (US$ Million)
Figure 8. Global Rare Disease Drug Market Share by Application in 2023 & 2030
Figure 9. Hospital Pharmacies
Figure 10. Speciality Pharmacies
Figure 11. Retail pharmacies
Figure 12. Others
Figure 13. Global Rare Disease Drug Revenue, (US$ Million), 2019 VS 2023 VS 2030
Figure 14. Global Rare Disease Drug Market Size (2019-2030) & (US$ Million)
Figure 15. Global Rare Disease Drug Sales (2019-2030) & (K Doses)
Figure 16. Global Rare Disease Drug Average Price (USD/Dose) & (2019-2030)
Figure 17. Rare Disease Drug Report Years Considered
Figure 18. Rare Disease Drug Sales Share by Manufacturers in 2023
Figure 19. Global Rare Disease Drug Revenue Share by Manufacturers in 2023
Figure 20. The Global 5 and 10 Largest Rare Disease Drug Players: Market Share by Revenue in 2023
Figure 21. Rare Disease Drug Market Share by Company Type (Tier 1, Tier 2 and Tier 3): 2019 VS 2023
Figure 22. Global Rare Disease Drug Market Size by Region (US$ Million): 2019 VS 2023 VS 2030
Figure 23. North America Rare Disease Drug Sales Market Share by Country (2019-2030)
Figure 24. North America Rare Disease Drug Revenue Market Share by Country (2019-2030)
Figure 25. U.S. Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 26. Canada Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 27. Europe Rare Disease Drug Sales Market Share by Country (2019-2030)
Figure 28. Europe Rare Disease Drug Revenue Market Share by Country (2019-2030)
Figure 29. Germany Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 30. France Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 31. U.K. Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 32. Italy Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 33. Russia Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 34. Asia Pacific Rare Disease Drug Sales Market Share by Region (2019-2030)
Figure 35. Asia Pacific Rare Disease Drug Revenue Market Share by Region (2019-2030)
Figure 36. China Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 37. Japan Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 38. South Korea Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 39. India Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 40. Australia Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 41. Taiwan Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 42. Indonesia Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 43. Thailand Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 44. Malaysia Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 45. Philippines Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 46. Latin America Rare Disease Drug Sales Market Share by Country (2019-2030)
Figure 47. Latin America Rare Disease Drug Revenue Market Share by Country (2019-2030)
Figure 48. Mexico Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 49. Brazil Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 50. Argentina Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 51. Middle East & Africa Rare Disease Drug Sales Market Share by Country (2019-2030)
Figure 52. Middle East & Africa Rare Disease Drug Revenue Market Share by Country (2019-2030)
Figure 53. Turkey Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 54. Saudi Arabia Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 55. U.A.E Rare Disease Drug Revenue Growth Rate (2019-2030) & (US$ Million)
Figure 56. Global Sales Market Share of Rare Disease Drug by Type (2019-2030)
Figure 57. Global Revenue Market Share of Rare Disease Drug by Type (2019-2030)
Figure 58. Global Rare Disease Drug Price (USD/Dose) by Type (2019-2030)
Figure 59. Global Sales Market Share of Rare Disease Drug by Application (2019-2030)
Figure 60. Global Revenue Market Share of Rare Disease Drug by Application (2019-2030)
Figure 61. Global Rare Disease Drug Price (USD/Dose) by Application (2019-2030)
Figure 62. Rare Disease Drug Value Chain
Figure 63. Rare Disease Drug Production Process
Figure 64. Channels of Distribution (Direct Vs Distribution)
Figure 65. Distributors Profiles
Figure 66. Bottom-up and Top-down Approaches for This Report
Figure 67. Data Triangulation
Figure 68. Key Executives Interviewed