Index
1 Market Overview of Hemophilia Gene Therapy
1.1 Hemophilia Gene Therapy Market Overview
1.1.1 Hemophilia Gene Therapy Product Scope
1.1.2 Hemophilia Gene Therapy Market Status and Outlook
1.2 Global Hemophilia Gene Therapy Market Size Overview by Region 2018 VS 2022 VS 2029
1.3 Global Hemophilia Gene Therapy Market Size by Region (2018-2029)
1.4 Global Hemophilia Gene Therapy Historic Market Size by Region (2018-2023)
1.5 Global Hemophilia Gene Therapy Market Size Forecast by Region (2024-2029)
1.6 Key Regions, Hemophilia Gene Therapy Market Size (2018-2029)
1.6.1 North America Hemophilia Gene Therapy Market Size (2018-2029)
1.6.2 Europe Hemophilia Gene Therapy Market Size (2018-2029)
1.6.3 Asia-Pacific Hemophilia Gene Therapy Market Size (2018-2029)
1.6.4 Latin America Hemophilia Gene Therapy Market Size (2018-2029)
1.6.5 Middle East & Africa Hemophilia Gene Therapy Market Size (2018-2029)
2 Hemophilia Gene Therapy Market by Type
2.1 Introduction
2.1.1 Hemophilia A
2.1.2 Hemophilia B
2.2 Global Hemophilia Gene Therapy Market Size by Type: 2018 VS 2022 VS 2029
2.2.1 Global Hemophilia Gene Therapy Historic Market Size by Type (2018-2023)
2.2.2 Global Hemophilia Gene Therapy Forecasted Market Size by Type (2024-2029)
2.3 Key Regions Market Size by Type
2.3.1 North America Hemophilia Gene Therapy Revenue Breakdown by Type (2018-2029)
2.3.2 Europe Hemophilia Gene Therapy Revenue Breakdown by Type (2018-2029)
2.3.3 Asia-Pacific Hemophilia Gene Therapy Revenue Breakdown by Type (2018-2029)
2.3.4 Latin America Hemophilia Gene Therapy Revenue Breakdown by Type (2018-2029)
2.3.5 Middle East and Africa Hemophilia Gene Therapy Revenue Breakdown by Type (2018-2029)
3 Hemophilia Gene Therapy Market Overview by Application
3.1 Introduction
3.1.1 Hemophilia A Gene Therapy
3.1.2 Hemophilia B Gene Therapy
3.2 Global Hemophilia Gene Therapy Market Size by Application: 2018 VS 2022 VS 2029
3.2.1 Global Hemophilia Gene Therapy Historic Market Size by Application (2018-2023)
3.2.2 Global Hemophilia Gene Therapy Forecasted Market Size by Application (2024-2029)
3.3 Key Regions Market Size by Application
3.3.1 North America Hemophilia Gene Therapy Revenue Breakdown by Application (2018-2029)
3.3.2 Europe Hemophilia Gene Therapy Revenue Breakdown by Application (2018-2029)
3.3.3 Asia-Pacific Hemophilia Gene Therapy Revenue Breakdown by Application (2018-2029)
3.3.4 Latin America Hemophilia Gene Therapy Revenue Breakdown by Application (2018-2029)
3.3.5 Middle East and Africa Hemophilia Gene Therapy Revenue Breakdown by Application (2018-2029)
4 Hemophilia Gene Therapy Competition Analysis by Players
4.1 Global Hemophilia Gene Therapy Market Size by Players (2018-2023)
4.2 Global Top Players by Company Type (Tier 1, Tier 2 and Tier 3) & (based on the Revenue in Hemophilia Gene Therapy as of 2022)
4.3 Date of Key Players Enter into Hemophilia Gene Therapy Market
4.4 Global Top Players Hemophilia Gene Therapy Headquarters and Area Served
4.5 Key Players Hemophilia Gene Therapy Product Solution and Service
4.6 Competitive Status
4.6.1 Hemophilia Gene Therapy Market Concentration Rate
4.6.2 Mergers & Acquisitions, Expansion Plans
5 Company (Top Players) Profiles
5.1 Spark Therapeutics
5.1.1 Spark Therapeutics Profile
5.1.2 Spark Therapeutics Main Business
5.1.3 Spark Therapeutics Hemophilia Gene Therapy Products, Services and Solutions
5.1.4 Spark Therapeutics Hemophilia Gene Therapy Revenue (US$ Million) & (2018-2023)
5.1.5 Spark Therapeutics Recent Developments
5.2 Ultragenyx
5.2.1 Ultragenyx Profile
5.2.2 Ultragenyx Main Business
5.2.3 Ultragenyx Hemophilia Gene Therapy Products, Services and Solutions
5.2.4 Ultragenyx Hemophilia Gene Therapy Revenue (US$ Million) & (2018-2023)
5.2.5 Ultragenyx Recent Developments
5.3 Shire PLC
5.3.1 Shire PLC Profile
5.3.2 Shire PLC Main Business
5.3.3 Shire PLC Hemophilia Gene Therapy Products, Services and Solutions
5.3.4 Shire PLC Hemophilia Gene Therapy Revenue (US$ Million) & (2018-2023)
5.3.5 Sangamo Therapeutics Recent Developments
5.4 Sangamo Therapeutics
5.4.1 Sangamo Therapeutics Profile
5.4.2 Sangamo Therapeutics Main Business
5.4.3 Sangamo Therapeutics Hemophilia Gene Therapy Products, Services and Solutions
5.4.4 Sangamo Therapeutics Hemophilia Gene Therapy Revenue (US$ Million) & (2018-2023)
5.4.5 Sangamo Therapeutics Recent Developments
5.5 Bioverativ
5.5.1 Bioverativ Profile
5.5.2 Bioverativ Main Business
5.5.3 Bioverativ Hemophilia Gene Therapy Products, Services and Solutions
5.5.4 Bioverativ Hemophilia Gene Therapy Revenue (US$ Million) & (2018-2023)
5.5.5 Bioverativ Recent Developments
5.6 BioMarin
5.6.1 BioMarin Profile
5.6.2 BioMarin Main Business
5.6.3 BioMarin Hemophilia Gene Therapy Products, Services and Solutions
5.6.4 BioMarin Hemophilia Gene Therapy Revenue (US$ Million) & (2018-2023)
5.6.5 BioMarin Recent Developments
5.7 uniQure
5.7.1 uniQure Profile
5.7.2 uniQure Main Business
5.7.3 uniQure Hemophilia Gene Therapy Products, Services and Solutions
5.7.4 uniQure Hemophilia Gene Therapy Revenue (US$ Million) & (2018-2023)
5.7.5 uniQure Recent Developments
5.8 Freeline Therapeutics
5.8.1 Freeline Therapeutics Profile
5.8.2 Freeline Therapeutics Main Business
5.8.3 Freeline Therapeutics Hemophilia Gene Therapy Products, Services and Solutions
5.8.4 Freeline Therapeutics Hemophilia Gene Therapy Revenue (US$ Million) & (2018-2023)
5.8.5 Freeline Therapeutics Recent Developments
6 North America
6.1 North America Hemophilia Gene Therapy Market Size by Country (2018-2029)
6.2 U.S.
6.3 Canada
7 Europe
7.1 Europe Hemophilia Gene Therapy Market Size by Country (2018-2029)
7.2 Germany
7.3 France
7.4 U.K.
7.5 Italy
7.6 Russia
7.7 Nordic Countries
7.8 Rest of Europe
8 Asia-Pacific
8.1 Asia-Pacific Hemophilia Gene Therapy Market Size by Region (2018-2029)
8.2 China
8.3 Japan
8.4 South Korea
8.5 Southeast Asia
8.6 India
8.7 Australia
8.8 Rest of Asia-Pacific
9 Latin America
9.1 Latin America Hemophilia Gene Therapy Market Size by Country (2018-2029)
9.2 Mexico
9.3 Brazil
9.4 Rest of Latin America
10 Middle East & Africa
10.1 Middle East & Africa Hemophilia Gene Therapy Market Size by Country (2018-2029)
10.2 Turkey
10.3 Saudi Arabia
10.4 UAE
10.5 Rest of Middle East & Africa
11 Hemophilia Gene Therapy Market Dynamics
11.1 Hemophilia Gene Therapy Industry Trends
11.2 Hemophilia Gene Therapy Market Drivers
11.3 Hemophilia Gene Therapy Market Challenges
11.4 Hemophilia Gene Therapy Market Restraints
12 Research Finding /Conclusion
13 Methodology and Data Source
13.1 Methodology/Research Approach
13.1.1 Research Programs/Design
13.1.2 Market Size Estimation
13.1.3 Market Breakdown and Data Triangulation
13.2 Data Source
13.2.1 Secondary Sources
13.2.2 Primary Sources
13.3 Disclaimer
13.4 Author List